The effects of Sanfilippo syndrome in small children are so devastating that the rare disease is often known as "childhood dementia." About one in 70,000 newborns inherit this disorder.

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Sanfilippo syndrome is a rare genetic disorder that affects the body's ability to break down complex sugars, causing symptoms of dementia in children. There is no cure, and the regression is ...

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In December 2021, Newsweek shared the story of Simon Croke – a 5-year-old boy diagnosed with Sanfilippo Syndrome, a fatal degenerative disease that presents symptoms similar to Alzheimer's. On ...

Sanfilippo syndrome is a terminal disease with no cure and no treatment. It affects one in 70,000 children and is a genetic condition that affects the metabolism of complex molecules and results ...

In March 2022, Olivia Stoop was diagnosed with Sanfilippo syndrome, a terminal genetic disorder Leading up to her daughter Olivia’s 2-year checkup, Erin Stoop couldn’t shake the feeling that ...

Eliza suffers from Sanfilippo syndrome–Type A, a rare and ultimately fatal genetic disorder that primarily affects the brain. The 5-year-old is slowly losing her ability to speak, ...

This is because on March 28, Liv was diagnosed with Sanfilippo Syndrome Type B, a rare disease that is compared to late-stage Alzheimer's, but for children. "It is 100% fatal," said Erin.

Torrance, California, June 21, 2024 (GLOBE NEWSWIRE) -- As a neurodegenerative disease characterized by childhood onset dementia, Sanfilippo syndrome causes immense suffering in many ways ...

Aiden Lopez has been diagnosed with a fatal genetic disorder called Sanfilippo syndrome.There may be a stem cell treatment that could treat him, but his health insurance denied coverage of the ...