The effects of Sanfilippo syndrome in small children are so devastating that the rare disease is often known as "childhood dementia." About one in 70,000 newborns inherit this disorder.

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Sanfilippo syndrome is a rare genetic disorder that affects the body's ability to break down complex sugars, causing symptoms of dementia in children. There is no cure, and the regression is ...

In December 2021, Newsweek shared the story of Simon Croke – a 5-year-old boy diagnosed with Sanfilippo Syndrome, a fatal degenerative disease that presents symptoms similar to Alzheimer's. On ...

Sanfilippo syndrome is a terminal disease with no cure and no treatment. It affects one in 70,000 children and is a genetic condition that affects the metabolism of complex molecules and results ...

After 4-year-old Eliza O'Neill was diagnosed last summer with Sanfilippo syndrome, a rare and fatal genetic disease, her parents, Glen and Cara, realized the real heartbreak wasn't actually the ...

In March 2022, Olivia Stoop was diagnosed with Sanfilippo syndrome, a terminal genetic disorder Leading up to her daughter Olivia’s 2-year checkup, Erin Stoop couldn’t shake the feeling that ...

This is because on March 28, Liv was diagnosed with Sanfilippo Syndrome Type B, a rare disease that is compared to late-stage Alzheimer's, but for children. "It is 100% fatal," said Erin.

Eliza suffers from Sanfilippo syndrome–Type A, a rare and ultimately fatal genetic disorder that primarily affects the brain. The 5-year-old is slowly losing her ability to speak, ...

Eliza has Sanfilippo syndrome type A, a rare genetic disorder that causes a deadly buildup of heparin sulfate in her cells. Soon, Eliza will lose the ability to speak, her parents say.

Torrance, California, June 21, 2024 (GLOBE NEWSWIRE) -- As a neurodegenerative disease characterized by childhood onset dementia, Sanfilippo syndrome causes immense suffering in many ways ...