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European regulators said that a Duchenne gene therapy should not be approved, imperiling the treatment that is also facing ...
The patient with Duchenne muscular dystrophy, who died in Brazil, was treated with Elevidys but was not a participant in a ...
The drug, which was designed to treat Duchenne muscular dystrophy, has been linked to the deaths of two teenage boys.
US regulators said they are investigating the death of an 8-year-old boy who received a gene therapy from Sarepta ...
Sarepta Therapeutics failed to win the European drug regulator's backing for its muscle disorder gene therapy on Friday, as ...
Genetic testing could not confirm Duchenne muscular dystrophy, but a muscle biopsy at UCLA did. "He could see that he was ...
The European drug authority recommends refusal of marketing authorization after study shows no benefit over placebo.
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