News

Sarepta Therapeutics is pausing shipments of its gene therapy for muscular dystrophy following several patient deaths that ...
The agency also revoked Sarepta's platform technology designation for AAVrh74 Friday and issued a safety communication saying ...
Using gene therapy to treat hereditary deafness is safe and effective in both children and adults, according to new ...
The Vision Center at Children’s Hospital Los Angeles is developing a protocol for a phase 1 clinical trial for the first gene ...
Youth with congenital deafness treated with gene therapy showed better progress on certain hearing measures than counterparts ...
Scientists have made major progress in treating congenital deafness using gene therapy. This approach repairs hearing loss by ...
KLOTHO NEUROSCIENCES, INC. - Gene and Cell Therapy of Longevity and Neurodegenerative Diseases. "AAV gene therapy has been proven to be a revolutionary one-time, life-changing treatment, however ...
Sarepta Therapeutics said it will temporarily pause all shipments of delandistrogene moxeparvovec (Elevidys) for Duchenne ...